bubble boy diseaseの例文

• The therapy cured nine babies afflicted with " bubble boy disease,"
• His immune system lay ravaged, a condition known as bubble boy disease, rendering his body unable to defend itself against the slightest infection.
• Bubble boy disease _ an immune disorder formally called severe combined immunodeficiency, or SCID _ is the only disease ever to be cured with gene therapy.
• Ironically, the new compound was inspired by the deadly " bubble boy disease, " in which children are born without a functioning immune system.
• "This includes so-called bubble boy disease, bone marrow storage diseases, sickle cell anemia, Fanconi's anemia, literally dozens more ."
• Abbreviated as SCID, but commonly called " bubble boy disease, " it is extremely rare and is fatal in the first year of life if left untreated.
• In 1990, the FDA approved Enzon's first drug, Adagen, for the treatment of severe combined immunodeficiency disease, commonly called " bubble boy disease ."
• The findings also could have implications for treating illnesses associated with a loss of infection-fighting cells, such as HIV and severe combined immunodeficiency, better known as bubble boy disease.
• In the most striking success yet for gene therapy, French doctors have apparently cured four little boys of the rare and deadly immune system disorder dubbed " bubble boy disease ."
• A revolutionary gene therapy treatment that cured 10 French boys of a deadly inherited disorder known as " bubble boy disease " definitely gave two of them leukemia, scientists said Sunday.
• The disorder is often called the " bubble boy disease " because a well-known Houston victim, known only as David, lived for years in a plastic bubble filled with filtered air.
• Within a month, he received a call from Kenneth Weinberg, the Los Angeles bone marrow transplant specialist who was treating the boy with bubble boy disease, known scientifically as severe combined immune deficiency, or SCID.
• In an exciting and long-awaited success, gene therapy has restored apparently normal immune systems to two French babies born with a rare, lethal immune disease sometimes called the " bubble boy disease ."
• A single injection of genetically modified stem cells is all it took to cure two children of a complex form of an inherited immune system disorder often referred to as the " bubble boy disease, " researchers report.
• In the most striking success yet for gene therapy, doctors in Paris essentially gave a healthy new immune system to the four babies, who were born with the rare, genetic immune disorder best known as " bubble boy disease ."
• Vetter, who died in 1984, is a symbol for children with SCID, the foundation says, and his lifelong isolation linked the nickname " Bubble Boy " with him and the term " Bubble Boy Disease " with SCID.
• A second European toddler apparently suffered a leukemia-like side effect from gene therapy that cured him of the rare but deadly " bubble boy disease, " prompting the government to suspend 27 more gene therapy studies while they investigate the risk.
• A French toddler suffering a leukemia-like side effect from gene therapy that was used to cure an immune disorder called " bubble boy disease " is doing well, but scientists said Thursday they still haven't pinpointed what caused his illness.
• GENE-LEUKEMIA ( Undated ) _ Gene therapy almost certainly caused a leukemia like disease in a three-year-old French boy with bubble boy disease who had been considered among the first success stories in gene therapy, scientists and federal officials concluded yesterday.
• A second European toddler apparently suffered a leukemia-like side effect from gene therapy that cured him of the rare but deadly " bubble boy disease, " prompting the government on Tuesday to suspend 27 more gene therapy studies while they investigate the risk.